Conditions & Recovery · STAT News · August 20, 2026

Opinion: Capricor’s Duchenne muscular dystrophy drug and the countless tiny decisions that can make or break a study

“Regulatory flexibility can be exercised in rare disease without sacrificing rigor,” writes Mindy Leffler, whose son has Duchenne muscular dystrophy.

Originally published by STAT News. We curate and add context; they did the reporting.

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